Discover the forefront of gene therapy at the 4th Gene Therapy for Muscular Disorders Summit (April 16-18, Boston). Following the groundbreaking approval of Sarepta's DMD gene therapy in June 2023, ...

Congenital muscular dystrophies (CMDs) comprise a heterogeneous group of inherited disorders primarily affecting muscle integrity and function, often with accompanying brain and ocular abnormalities.

I've been blogging for a few years about misophonia, an auditory/neurological disorder that I have advocated for because I and (more importantly) one of my adult children are affected. Recently, at ...

A team has discovered a possible therapeutic approach to repair injured muscles either from aging or degenerative muscle disorders. For millions of people, losing muscle isn't just about weakness; ...

When it comes to muscular diseases, most of us have heard of especially common ones like muscular dystrophy and Lou Gehrig's disease. But one of the rarest muscular disorders is also one of the most ...

Congenital muscular dystrophy (CMD) is a disease that affects certain muscles. Individuals with CMD may experience symptoms such as muscle weakness and joint problems. “Congenital” means present since ...

Myasthenia gravis, or MG, is "a chronic autoimmune neuromuscular disorder that causes muscle weakness and fatigue," says Hesterlee. It occurs "when a person’s immune system is essentially attacking ...

A musculoskeletal disorder involves injuries or disorders to the muscles, nerves, tendons, joints, cartilage, and spinal discs. These conditions can cause pain, stiffness, weakness, and limitations in ...